PatientCrossroads CMD


Congenital Myasthenic Syndrome: Expanded Access Study of Amifampridine Phosphate

Primary Objective:
To provide patients with LEMS/CMS/downbeat nystagmus access to amifampridine phosphate therapy where physicians would like to treat with amifampridine phosphate
Secondary Objective:
To assess the long-term safety of amifampridine phosphate in patients with LEMS/CMS/downbeat nystagmus
Catalyst Pharmaceutical Partners, Inc
Voisin Consulting Life Sciences, Inc.
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