PatientCrossroads CMD


           

CMDIR Subtypes

Congenital Muscular Dystrophy subtypes included in the CMDIR

  • Alpha 7 Integrin Related Myopathy
  • Alpha 9 Integrin Related Myopathy
  • Collagen VI Related Myopathy (Ullrich through Bethlem CMD)
  • Alpha-Dystroglycan Related Muscular Dystrophy (Dystroglycanopathy, WWS, MEB, Fukuyama, FKRP, LGMD2I, LGMD2K, LGMD2M, LGMD2N, LGMD2O)
  • Choline Kinase B Receptor
  • LAMA2 Related Muscular Dystrophy (Laminin Alpha 2 related dystrophy/MDC1A/Merosin deficient)
  • LMNA Related Muscular Dystrophy (Laminopathy/LaminA/C, L-CMD, Emery Dreifuss muscular dystrophy)
  • SEPN1 Related Myopathy (Rigid Spine Muscular Dystrophy/RSMD1, Congenital Fiber Type Disproportion, Mallory Weiss Body Desmin, Multi-minicore Myopathy)
  • SYNE1 (Nesprin Related Muscular Dystrophy)
  • Telethonin Related Muscular Dystrophy (TCAP/Titin-Cap)
  • CMD Undiagnosed (including Merosin Positive)

Congenital Myopathy subtypes included in CMDIR

  • Actin aggregation myopathy
  • Cap disease
  • Central core disease
  • Centronuclear myopathy
  • Congenital fiber type disporportion
  • Core rod myopathy
  • Hyaline body myopathy
  • Multiminicore myopathy
  • Myotubular myopathy
  • Nemaline myopathy
  • Reducing body myopathy
  • Spheroid body myopathy
  • Tubular aggregate myopathy
  • Zebra body disease myopathy
  • Congenital Myopathy with unknown subtype

Congenital Myasthenic Syndrome (all subtypes included in CMDIR)